News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
A Combination of Tests Shows Learning Capabilities of Nonverbal Children with Rare Brain Disorder
February 25, 2025 - NCATS News
- Our Impact on Rare Diseases
- Rare Diseases Clinical Research Network (RDCRN)
NCATS-funded scientists found that a pair of tests can measure nonverbal learning skills and show the cognitive abilities of children with Aicardi-Goutières syndrome. The tests could improve the support and therapy doctors provide.
Read ArticleAI Tool Helps Find Life-Saving Medicine for Rare Disease
February 5, 2025 - Grantee/Partner News
- Biomedical Data Translator (Translator)
- Our Impact on Rare Diseases
Rare Disease Congressional Caucus to Host Virtual Briefing: Economic Burden of Rare Diseases in America on Feb. 25, 2021
February 17, 2021 - Media Coverage
- Genetic and Rare Diseases (GARD) Information Center
Data Ownership as Leverage in Accelerating Rare Disease Drug Development
February 15, 2021 - Media Coverage
- Genetic and Rare Diseases (GARD) Information Center
Sandoz Launches Generic Icatibant in US for Rare Disease Hereditary Angioedema, Strategically Enhancing Injectables Portfolio
January 28, 2021 - Grantee/Partner News
- Genetic and Rare Diseases (GARD) Information Center
How Rare is This?
January 18, 2021 - Grantee/Partner News
- Genetic and Rare Diseases (GARD) Information Center
Physicians Have New Guidelines for Managing Rare Genetic, Metabolic Disorders
December 31, 2020 - Media Coverage
- Rare Diseases Clinical Research Network (RDCRN)
PaVe-GT: Collaborative NIH Effort Aimed at Creating a Gene Therapy Playbook, Making Rare Disease Treatments More Accessible
November 30, 2020 - NCATS News
- Our Impact on Rare Diseases
- Platform Vector Gene Therapy (PaVe-GT)
The Platform Vector Gene Therapy (PaVe-GT) initiative aims to make gene therapy development and clinical testing more streamlined and less expensive — and potentially more accessible to millions of