News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.

A Combination of Tests Shows Learning Capabilities of Nonverbal Children with Rare Brain Disorder
February 25, 2025 - NCATS News
- Our Impact on Rare Diseases
- Rare Diseases Clinical Research Network (RDCRN)
NCATS-funded scientists found that a pair of tests can measure nonverbal learning skills and show the cognitive abilities of children with Aicardi-Goutières syndrome. The tests could improve the support and therapy doctors provide.
Read ArticleAI Tool Helps Find Life-Saving Medicine for Rare Disease
February 5, 2025 - Grantee/Partner News
- Biomedical Data Translator (Translator)
- Our Impact on Rare Diseases
Cost of Rare Diseases in US? Nearly $1 Trillion in 2019, EveryLife Foundation Finds
March 30, 2021 - Media Coverage
- Genetic and Rare Diseases (GARD) Information Center
NCATS Researchers’ New Approach to Measure Gene Activity Could Speed Search for Rare Disease Therapies
March 23, 2021 - NCATS News
- Our Impact on Research Operations
NCATS scientists design an innovative test to find potential treatments for Charcot-Marie-Tooth disease (CMT), one of the most common inherited neurological diseases, opening new pathways for rare
COVID's All-Hands-on-Deck Approach Should Be Standard for Rare Diseases
March 18, 2021 - Media Coverage
- COVID-19
Pandemic Perspectives: NCATS Director Urges Rare Disease Community to Push against Return to Clinical Trial Status Quo
March 9, 2021 - Media Coverage
- COVID-19
Pandemic Perspectives: US FDA, NIH Tried to Be Flexible to Keep Rare Disease Trials Going
March 9, 2021 - Media Coverage
- COVID-19
How Covid-19 Is Changing Rare Diseases Research
March 9, 2021 - Media Coverage
- COVID-19
Twenty years after researchers published their first discoveries associated with human genome sequencing, policymakers are fighting to overcome obstacles that hobble the potential of genetic medici