News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
A Combination of Tests Shows Learning Capabilities of Nonverbal Children with Rare Brain Disorder
February 25, 2025 - NCATS News
- Our Impact on Rare Diseases
- Rare Diseases Clinical Research Network (RDCRN)
NCATS-funded scientists found that a pair of tests can measure nonverbal learning skills and show the cognitive abilities of children with Aicardi-Goutières syndrome. The tests could improve the support and therapy doctors provide.
Read ArticleAI Tool Helps Find Life-Saving Medicine for Rare Disease
February 5, 2025 - Grantee/Partner News
- Biomedical Data Translator (Translator)
- Our Impact on Rare Diseases
Pfizer, Novartis Sign on to Accelerate Gene Therapies for Rare Diseases with US Agencies
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
FDA, NIH Announce Bespoke Gene Therapy Consortium to Focus on Rare Diseases
October 28, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
A Rare Disease Diagnosis Comes with Significant Health Care Costs, Study Shows
October 28, 2021 - Media Coverage
- Our Impact on Rare Diseases
FDA, NIH, and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 27, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
NIH, FDA and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
October 27, 2021 - NCATS News
- Bespoke Gene Therapy Consortium (BGTC)
- Platform Vector Gene Therapy (PaVe-GT)
NIH, FDA and 15 private organizations partnered to create the Bespoke Gene Therapy Consortium to speed development of FDA-approved gene therapies for rare diseases.
Public-Private Partnership Launched to Accelerate Gene Therapies for Rare Diseases
October 27, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
The National Institutes of Health and U.S.