News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.
A Combination of Tests Shows Learning Capabilities of Nonverbal Children with Rare Brain Disorder
February 25, 2025 - NCATS News
- Our Impact on Rare Diseases
- Rare Diseases Clinical Research Network (RDCRN)
NCATS-funded scientists found that a pair of tests can measure nonverbal learning skills and show the cognitive abilities of children with Aicardi-Goutières syndrome. The tests could improve the support and therapy doctors provide.
Read ArticleAI Tool Helps Find Life-Saving Medicine for Rare Disease
February 5, 2025 - Grantee/Partner News
- Biomedical Data Translator (Translator)
- Our Impact on Rare Diseases
Drug Repurposing Approaches Reveal HIV Drug Holds Promise Against a Rare, Disabling Muscle Disorder
November 30, 2021 - NCATS News
Using drug repurposing approaches, researchers from NCATS, Duke University and the University of Florida discovered that an existing antiviral drug used against HIV infection may be helpful in trea
The BGTC is Working to Streamline the Development of Gene Therapies for Rare Diseases
November 23, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Hesperos Validates Utility of Human-on-a-Chip® Approach to Model Rare Autoimmune Disease, Myasthenia Gravis
November 22, 2021 - Grantee/Partner News
- Tissue Chip for Drug Screening
The Role of Gene Therapy in Curing Rare Diseases
November 18, 2021 - Media Coverage
FDA, NIH, and 15 Private Organizations Join Forces to Increase Effective Gene Therapies for Rare Diseases
November 17, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
ICD Codes and Rare Diseases
November 16, 2021 - Media Coverage
- Our Impact on Rare Diseases