News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.

A Combination of Tests Shows Learning Capabilities of Nonverbal Children with Rare Brain Disorder
February 25, 2025 - NCATS News
- Our Impact on Rare Diseases
- Rare Diseases Clinical Research Network (RDCRN)
NCATS-funded scientists found that a pair of tests can measure nonverbal learning skills and show the cognitive abilities of children with Aicardi-Goutières syndrome. The tests could improve the support and therapy doctors provide.
Read ArticleAI Tool Helps Find Life-Saving Medicine for Rare Disease
February 5, 2025 - Grantee/Partner News
- Biomedical Data Translator (Translator)
- Our Impact on Rare Diseases
Boost for NC Gene Therapy Companies – A New Rare Disease Consortium
December 20, 2021 - Media Coverage
- Bespoke Gene Therapy Consortium (BGTC)
Dr. Anne Pariser Provides an Overview of NIH’s Office of Rare Diseases Research
December 20, 2021 - Media Coverage
Gene Therapy Consortium Provides New Hope for Rare Disease Suffers
December 16, 2021 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Not So Rare Diseases: The Cumulative Burden of Underdiagnosis
December 14, 2021 - Media Coverage
NCATS’ Office of Rare Diseases Research Director Anne R.
Dr Anne Pariser Provides an Overview of NIH’s Office of Rare Diseases Research
December 1, 2021 - Media Coverage
Human-on-a-Chip Approach Validated to Model Rare Autoimmune Disease
November 30, 2021 - Media Coverage
- Tissue Chip for Drug Screening