News
Explore the latest stories and publications from NCATS and our partners, see upcoming events, or explore the variety of resources we provide to better understand translational science and our work.
News
Read the latest news from NCATS and its collaborators whose research is supported through the Center’s programs, or follow coverage of NCATS' translational research activities through national and local media.

A Combination of Tests Shows Learning Capabilities of Nonverbal Children with Rare Brain Disorder
February 25, 2025 - NCATS News
- Our Impact on Rare Diseases
- Rare Diseases Clinical Research Network (RDCRN)
NCATS-funded scientists found that a pair of tests can measure nonverbal learning skills and show the cognitive abilities of children with Aicardi-Goutières syndrome. The tests could improve the support and therapy doctors provide.
Read ArticleAI Tool Helps Find Life-Saving Medicine for Rare Disease
February 5, 2025 - Grantee/Partner News
- Biomedical Data Translator (Translator)
- Our Impact on Rare Diseases
Researchers Create 3-D Model for Rare Neuromuscular Disorders, Setting Stage for Clinical Trial
April 20, 2022 - Media Coverage
- Small Business (SBIR)
- Tissue Chip for Drug Screening
Researchers Create 3-D Model for Rare Neuromuscular Disorders, Setting Stage for Clinical Trial
April 19, 2022 - NCATS News
- Small Business (SBIR)
- Tissue Chip for Drug Screening
Partially funded by a Small Business Innovation Research grant from NCATS, Hesperos, Inc., researchers created a tissue chip model that mimics the biology of two rare neuromuscular disorders, setti
Hesperos Shows Potential for In Vitro Approach to Replace Conventional Animal Efficacy Studies for Rare Neuromuscular Disorders
April 19, 2022 - Grantee/Partner News
- Small Business (SBIR)
- Tissue Chip for Drug Screening
NCATS Aims to Transform Rare Disease Research
April 15, 2022 - Grantee/Partner News
- Our Impact on Rare Diseases
The National Economic Burden of Rare Disease Study
April 12, 2022 - Grantee/Partner News
- Bespoke Gene Therapy Consortium (BGTC)
Examining the Burden of Rare Diseases in the US
March 31, 2022 - Media Coverage
- Genetic and Rare Diseases (GARD) Information Center